abbreviation
- MOL THER
MOLECULAR THERAPY
Journal
Overview
publication venue for
- Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa. 30:2680-2692. 2022
- Correction of recessive dystrophic epidermolysis bullosa by homology-directed repair-mediated genome editing. 29:2008-2018. 2021
- Clinically Relevant Correction of Recessive Dystrophic Epidermolysis Bullosa by Dual sgRNA CRISPR/Cas9-Mediated Gene Editing. 27:986-998. 2019
- CRISPR/Cas9-Mediated In Situ Correction of LAMB3 Gene in Keratinocytes Derived from a Junctional Epidermolysis Bullosa Patient. 26:2592-2603. 2018
- Long-term skin regeneration from a gene-targeted human epidermal stem cell clone. 22:1878-1880. 2014
- Tropism-modified AAV vectors overcome barriers to successful cutaneous therapy. 22:929-939. 2014
- Targeted gene addition in human epithelial stem cells by zinc-finger nuclease-mediated homologous recombination. 21:1695-1704. 2013
- Preclinical corrective gene transfer in Xeroderma pigmentosum human skin stem cells. 20:798-807. 2012
- Ex-vivo gene therapy restores LEKTI activity and corrects the architecture of Netherton syndrome-derived skin grafts. 19:408-416. 2011
- Correction of laminin-5 deficiency in human epidermal stem cells by transcriptionally targeted lentiviral vectors. 16:1977-1985. 2008
International Standard Serial Number (ISSN)
- 1525-0016
Electronic International Standard Serial Number (EISSN)
- 1525-0024